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IUGT (in utero gene transfer)

Used to correct genetic defects of somatic cells by transfer of gene(s) into the unborn fetus. Its advantage is that it can be applied early during embryonic development before irreversible damage occurs, e.g., in various neurological diseases (Tay-Sachs, Niemann-Pick, Lesh-Nyhan, Sandhoff, Leigh, leukodystrophies, gangliosidoses, immunological disorders, thalassemias, osteopetrosis).